Trials and studies underway or in preparation in France
Taking part in a clinical trial can provide an opportunity to benefit from innovative treatments and contribute to scientific research. Here is a table of clinical trials currently underway or in preparation for mitochondrial diseases in France.

Trials underway or in preparation
Ongoing recruitment
More information about this trial: MELASMELAS
Medication: Sonlicromanol (KH176-301)
Ongoing recruitment
More information about this trial: MELASMELAS
Medication: TTI-0102
Ongoing recruitment
More information about this trial: Thymidine kinase 2 (TK2d) deficiencyThymidine kinase 2 (TK2d) deficiency
Medication: MT-1621 Compassionate Use Access
Upcoming recruitment
More information about this trial: Autosomal dominant optic atrophy (OPA1 gene)Autosomal dominant optic atrophy (OPA1 gene)
Medication: Natural history study
Ongoing recruitment
More information about this trial: Mitochondrial diseases (Multiple)Mitochondrial diseases (Multiple)
Medication: Immune dysfunctions (MitoID study)
Ongoing recruitment
More information about this trial: Friedreich's ataxiaFriedreich's ataxia
Medication: Natural History (Unifai Study)
Ongoing recruitment
More information about this trial: Friedreich's ataxiaFriedreich's ataxia
Medication: Real-world data collection (Profa study)
Ongoing recruitment
More information about this trial: Leber hereditary optic neuropathyLeber hereditary optic neuropathy
Medication: Metabolic analysis (MetabOCT study)
Ongoing recruitment
More information about this trial: Mitochondrial myopathies (multiple)Mitochondrial myopathies (multiple)
Medication: Home-based physical training and remote monitoring (TELE-MIT trial)