Trials and studies underway or in preparation in France
Taking part in a clinical trial can provide an opportunity to benefit from innovative treatments and contribute to scientific research. Here is a table of clinical trials currently underway or in preparation for mitochondrial diseases in France.
Trials underway or in preparation
MELAS
TTI-0102
Age:
From 16 to 60 years old
Location:
Angers
Thymidine kinase 2 (TK2d) deficiency
MT-1621 Compassionate Use Access
Age:
All ages
Autosomal dominant optic atrophy (OPA1 gene)
Natural history study
Age:
From 8 years old
Location:
Rennes
Mitochondrial diseases (Multiple)
Immune dysfunctions (MitoID study)
Age:
From 6 years old
Location:
Bordeaux, Toulouse
Friedreich's ataxia
Natural History (Unifai Study)
Age:
All ages
Location:
Paris, Strasbourg
Friedreich's ataxia
Real-world data collection (Profa study)
Age:
From 12 years old
Location:
Paris
Leber hereditary optic neuropathy
Metabolic analysis (MetabOCT study)
Age:
From 18 to 60 years old
Location:
Paris
Mitochondrial myopathies (multiple)
Home-based physical training and remote monitoring (TELE-MIT trial)
Age:
From 18 years old
Location:
Nice
Mitochondrial diseases (multiple)
KL1333 (Falcon trial)
Age:
From 18 years old
Location:
Bordeaux, Lille, Nice, Paris